Treatable Diseases

Today, there are many diseases that can be treated with umbilical cord blood stem cells. As research advances, the list will continue to grow and many more treatments and cures will be developed from this source as well as from dental pulp and adipose tissue. Below is a list of treatable disease with each type of stem cell source:

Treatable with umbilical cord blood stem cells

Blood Disorders / Hemoglobinopathies

  • Sickle-cell anemia (hemoglobin SS)
  • HbSC disease
  • Sickle βo Thalassemia
  • α-thalassemia major (hydrops fetalis)
  • β-thalassemia major (Cooley’s anemia)
  • β-thalassemia intermedia
  • E-βo thalassemia
  • E-β+ thalassemia

Blood Disorders / Hemoglobinopathies

  • Sickle-cell anemia (hemoglobin SS)
  • HbSC disease
  • Sickle βo Thalassemia
  • α-thalassemia major (hydrops fetalis)
  • β-thalassemia major (Cooley’s anemia)
  • β-thalassemia intermedia
  • E-βo thalassemia
  • E-β+ thalassemia

Other Diseases

  • Langerhans Cells Hystocitosys
  • Evan Syndrome
  • Family Hemofagocytic Lymphohistocitosys
  • Hemofagocytic Lymphohistocitosys Linked to the Epstein Barr Virus

Under Regenerative Clinical Trials

  • Cerebral Palsy
  • Neonatal Brain Injury
  • Type I Diabetes


  • Acute lymphoblastic leukemia (ALL)
  • Acute myeloid leukemia (AML)
  • Burkitt’s lymphoma
  • Chronic myeloid leukemia (CML)
  • Juvenile myelomonocytic leukemia (JMML)
  • Hemophagocytic lymphohistiocytosis
  • Non-Hodgkin’s lymphoma
  • Hodgkin’s lymphoma
  • Langerhans cell histiocytosis
  • Lymphomatoid granulomatosis
  • Myelodysplastic syndrome (MDS)
  • Chronic myelomonocytic leukemia (CMML

Metabolic Disorders

  • Adrenoleukodystrophy
  • Gaucher’s disease (infantile)
  • Metachromatic leukodystrophy
  • Krabbe disease (globoid cell leukodystrophy)
  • Gunther disease
  • Hermansky-Pudlak syndrome
  • Hurler syndrome
  • Hurler-Scheie syndrome
  • Hunter syndrome
  • Sanfilippo syndrome
  • Maroteaux-Lamy syndrome
  • Mucolipidosis Type II, III
  • Alpha mannosidosis
  • Niemann Pick Syndrome, type A and B
  • Sandhoff Syndrome
  • Tay-Sachs Disease
  • Batten disease (inherited neuronal ceroid lipofuscinosis)
  • Lesch-Nyhan disease


  • Ataxia telangiectasia
  • Chronic granulomatous disease
  • DiGeorge syndrome
  • IKK gamma deficiency
  • Immune dysregulation polyendocrineopathy X-linked
  • Mucolipidosis, Type II
  • Myelokathexis
  • X-linked immunodeficiency
  • Severe combined immunodeficiency
  • Adenosine deaminase deficiency
  • Wiskott-Aldrich syndrome
  • X-linked agammaglobulinemia
  • X-linked lymphoproliferative disease
  • Omenn’s syndrome
  • Reticular dysplasia
  • Thymic dysplasia
  • Leukocyte adhesion deficiency

Bone Marrow Failure Syndromes

  • Amegakaryocytic thrombocytopenia
  • Autoimmune neutropenia (severe)
  • Congenital dyserythropoietic anemia
  • Cyclic neutropenia
  • Diamond-Blackfan anemia
  • Evan’s syndrome
  • Fanconi anemia
  • Glanzmann’s disease
  • Juvenile dermatomyositis
  • Kostmann’s syndrome
  • Red cell aplasia
  • Schwachman syndrome
  • Severe aplastic anemia
  • Congenital sideroblastic anemia
  • Thrombocytopenia with absent radius (TAR syndrome)
  • Dyskeratosis congenita

Even though the applications of umbilical cord blood and cord tissue stem cells are increasing, it is unlikely that a relative who does not suffer from these diseases would need the stem cells obtained from the original donor. There are no guarantees that these stem cells may be compatible or that it may produce a cure.

The stem cells from umbilical cord blood and cord tissue do not guarantee successful treatments for all genetic diseases. As in any other transplant therapy, the efficacy of the therapy depends not only on the stem cells themselves but on many other factors such as the compatibility between the recipient and the donor.

GeneCell International is one of the leaders in the field of stem cell banking. We operate a laboratory that focuses on processing and cryopreserving of stem cells derived from umbilical cord blood, adipose tissue, other tissues, and cells that can be cryogenically preserved. Our purpose is to provide families with the highest quality stem cell products and services and the best customer service, unparalleled scientific excellence and innovative leadership in the areas of stem cell collection, processing and cryopreservation.

GeneCell International, with more than 15 years of experience, uses state-of-the-art equipment and highly qualified personnel for processing and storing stem cells.

GeneCell International’s mission is to educate the public about the benefits of cryopreserving Stem Cells and locate private or public banks worldwide so each and every day more people can have access to a transplant, in a timely manner, to meet their health needs. For more information visit:

Social Networks